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BioMarin Strengthens Enzyme Therapy Business with Acquisition of Inozyme Pharma
BMRNBioMarin Pharmaceutical(BMRN) Prnewswire·2025-05-16 11:30

Acquisition is Strong Strategic Fit for BioMarin, Adding INZ-701, a Phase 3 Enzyme Replacement Therapy Being Developed for Treatment of ENPP1 DeficiencyFirst Pivotal Data Readout in Children Expected in Early 2026 with Potential Launch in 2027; Additional Clinical Programs to Expand to Patients of all Ages Potential First-in-Disease Treatment for ENPP1 DeficiencyConference Call and Webcast Scheduled Today at 8:45 a.m. ETSAN RAFAEL, Calif. and BOSTON, May 16, 2025 /PRNewswire/ -- BioMarin Pharmaceutical Inc. ...